The FDA has granted fast track designation to DYNE-101, a therapy for myotonic dystrophy type 1 (DM1) now in testing in a ...

A pilot study in 19 LGMD patients and one with Becker MD found low-dose prednisone helped lower markers of muscle damage and ...

An accident and a malfunction render both of columnist Betty Vertin's accessible vans useless, leaving the family without transportation.

The investigational therapy DYNE-101 worked as expected and led to functional improvements for people with myotonic dystrophy type 1 (DM1) in a clinical trial, according to an update from developer ...

Many times over the years since the 1989 car crash that nearly killed me, I’ve been asked if I had any near-death or out-of-body experiences while I hung between life and death. I always try to ...

Note: This story was updated Jan. 17, 2025, to clarify the company’s comments on gene therapies, which generally deliver a smaller form of dystrophin. This designation aims to encourage the ...

In August 1985, I was diagnosed with Becker muscular dystrophy. So the doctors focused on the Becker type, as the majority of my presenting symptoms were similar to Duchenne’s. These included having ...