In addition, I think the recognition across all diseases where not everyone is going to be an expert in FA, and people can refer readily to tertiary care centers and even ordinary care centers that ...

Anthony Monaco was a very active teen—involved in soccer, wrestling, and even cross country—but he always felt a little awkward physically. It started with running a little differently than the kids ...

Health Canada has granted approval for Biogen’s Skyclarys (omaveloxolone) to treat Friedreich’s ataxia (FA), a rare, ...

Dunlavin was alive with the sounds of music and song when the community came together at St Nicholas Church of Ireland for a ...

In this video David Lynch, MD, PhD, discusses the effect Friedreich's ataxia can have on patients' quality of life.

Solid Biosciences Inc. (Nasdaq: SLDB) (the "Company”), a life sciences company developing precision genetic medicines for ...

PTC's diversified pipeline, including vatiquinone for Friedreich's ataxia, could significantly enhance revenue if approved, targeting a $2.8 billion market. Financial risks remain due to reliance ...