During 2024, SPINRAZA remained the primary source of ... And that is in time and in sequence with what we are doing for the regulatory process for the anticipated approval on August 21.

Now in occasions with a particularly novel area, you may sometimes be able to amend or alter expression and SPINRAZA is a good ... So you are targeting non coding sequence and then my guess ...

As its name suggests, splicing involves snipping out certain sequences in the RNA called ... disorder spinal muscular atrophy (SMA) – Spinraza (nusinersen) – is one result of that effort.

Spinraza (nusinersen) is an injection therapy widely approved ... While humans also have SMN2, a so-called backup gene for SMN1, a slight difference in its DNA sequence results in an event called ...

Not only does the company have Spinraza, it also sells the Friedreich’s ataxia ... It’s designed to bind to select sequences of RNA to increase the expression of a sodium channel protein tied to ...

Shane here! I just wanted to quick put up some reflections on my day today. I got my 7th Spinraza injection and it was quite a long day! Manfred considering petition to have Rose posthumously ...

So if you plan to call it quits at work within a decade, or you’ve just retired, you may want to take steps to minimize what’s called sequence risk, which is the risk that the market falls ...

Spinal muscular atrophy (SMA) therapy Spinraza has been a key earner for Biogen in recent years, but with sales now heading into reverse, the company is looking to extend its franchise.