In its early weeks, an animal embryo undergoes an incredibly delicate and intricate transformation. Cells grow, divide their genetic material, and separate themselves into brain cells, heart cells, ...

Case Western Reserve University researchers combine novel chemical method with CRISPR gene-editing tools to target disease-specific versions of genetic code The gene-editing technique known as CRISPR ...

Alternative splicing is a genetic process where different segments of genes are removed, and the remaining pieces are joined together during transcription to messenger RNA (mRNA). This mechanism ...

A new genome-wide mapping method finally shows how thousands of genes connect to drive disease. Biomedical researchers are working intensively to identify the genes that contribute to disease, with ...

Biotechnology start-ups are often advised to think early about process design to avoid hiccups during scaleup. A clinical-stage gene-therapy developer has taken this approach to heart, saying they’ve ...

Alternative splicing is a genetic process where different segments of genes are removed, and the remaining pieces are joined together during transcription to messenger RNA (mRNA). This mechanism ...

U.K.-based Cell and Gene Therapy Catapult (CGT Catapult) opened a new laboratory in Stevenage which has been specifically designed and equipped to allow cell and gene therapy developers to monitor and ...

With the FDA expecting to approve 10–20 Cell and Gene Therapies (CGTs) annually by 2025, it is evident that the field will continue to hold immense commercial and medical opportunities. To harness ...

Gene therapy has the potential to dramatically benefit patients with genetic blood disorders, but a small study on participants in a clinical trial for sickle cell disease suggests that a key process ...

A Stanford University biochemist who has greatly advanced human understanding of how cells copy themselves, and what controls the process, will receive the 2001 Welch Award tonight. Roger Kornberg, 54 ...